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https://www.contemporarypediatrics.com/view/fda-approves-first-gene-therapy-to-treat-pediatric-patients-with-duchenne-muscular-dystrophy
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First Gene Therapy to Treat Pediatric Duchenne Muscular Dystrophy Approved by FDA - Drug Topics
6/23/23 at 4:13pm
Organization
Contemporarypediatrics.com
Author
Joshua Fitch
Details
39 words
Summarize
Genetic Disorders
Business & Industrial
Gene Therapy
DMD
FDA
moxeparvovec-rokl
ELEVIDYS
Sarepta
micro-dystrophin
The accelerated approval of delandistrogene moxeparvovec-rokl is “based on expression of Elevidys micro-dystrophin observed in patients treated with ELEVIDYS,” according to Sarepta Therapeutics.
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