https://www.bmj.com/content/380/bmj.p370
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2/15/23 at 9:48am
Organization
The BMJ
Authors
A 19 month old child named Teddi has received life saving gene therapy treatment for metachromatic leukodystrophy (MLD)—a disorder that causes severe damage to the nervous system and organs—in an NHS first.
The one time treatment, Libmeldy (atidarsagene auto…
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