https://www.contemporarypediatrics.com/view/gene-therapy-improves-auditory-response-for-child-with-profound-genetic-hearing-loss
A child with profound genetic hearing loss was dosed with the investigational otoferlin gene therapy (DB-OTO), becoming the first patient dosed in a phase 1/2 trial evaluating the treatment, and experienced improved auditory response at week 6 with no concern…
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