https://www.washingtonpost.com/dc-md-va/2023/12/02/rare-condition-sanfilippo-fda/
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12/2/23 at 4:43pm
Organization
The Washington Post
Author
Theresa Vargas
Jill Wood and others who know the way Sanfilippo syndrome devastates families hope to convince the FDA to grant treatments accelerated approval.
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